Sickle cell anemia

Sickle cell anemia is an inherited blood disorder that causes the hemoglobin in red blood cells to form abnormally, giving the cells a crescent or sickle shape. In 2023, the FDA approved a new treatment for sickle cell anemia that edits the patient's DNA, correcting the genetic defect and completely curing the disease. The tool enabling this genetic editing is called CRISPR-Cas9. However, at this stage, the medical procedure is extremely expensive, complex, and lengthy.